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Efficacy and Safety of a Novel RPGROFR15 Gene Therapy (FT-002) for the Treatment of RPGR-Associated XLRP
27th ASGCT
Zhong-Dong SHI|2024-05
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Developing an AAV-based Gene Therapy for MYBPC3 Mutation-Associated Hypertrophic Cardiomyopathy
27th ASGCT
Therese S. Salameh |2024-05
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AAV KP1 Efficiently Transduces Human Cell Lines in vitro and Mouse Liver but not Non-Human Primate Liver after Intravenous Injection
27th ASGCT
Zhong-Dong SHI|2024-05